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Publications du laboratoire Translational Research in Gene Therapy (UMR_S 1089-TARGET)

 

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Click chemistry ABCA4 Dystrophin Homogeneity Vector Gene Transfer Antibodies/immunology/metabolism Baculovirus Discriminant analysis Immune response Mice Analytical ultracentrifugation Tolerance Gene transfer Genes Fluid-air exchange AAV vectors Crigler–Najjar Syndrome Assembly-activating protein AAV vector Dose study Gene Therapy Engineering GRMD dog Immunogenicity Canaux transient receptor potential Identity assay Childhood blindness High-throughput sequencing Gene-therapy Skeletal muscle Adenoassociated viral vector Air tamponade Calcium Capsid assembly Congenital amaurosis Insect cells AAP Manufacturing Capsid thermostability Chimie des sucres Gait assessment Treg Gene therapy Age DMD GRMD Adenoviridae/immunology Quality control Bioorthogonality Next generation sequencing DMDmdx rat Cell therapy Human-monocyte-derived dendritic cells CNS Centronuclear myopathy Bioconjuguaison Eye surgery Baculovirus expression vector Ciblage Cone photoreceptors GC-content Humoral immunity Beta-subunit Animals Homologous recombination Cell–virus interaction Exon skipping Immune responses AAV Inflammation Bioconjugates Duchenne CMC High-throughput technology Impurities Capsid thermal stability Antibody responses Cerebellum Homopolymers Clinical trials Clinical trial Bioconjugation Adeno-associated virus Accelerometry Acute treatment Carbohydrate Chemistry AUC Ectopic expression Immunogenicity inflammation gene therapy AAV Identity CD8 + T lymphocytes B-Lymphocytes/immunology/metabolism Capsid Duchenne muscular dystrophy Dynamin 2 Immunosuppression Animal model Immunomodulation Exercise